The cost-effectiveness of enzyme replacement therapy (ert) for the infantile form of pompe disease: comparing a high-income country’s approach (england) to that of a middleincome one (colombia)
Objectives Determining the cost-effectiveness of enzyme replacement therapy (ERT) for the classical infantile form of Pompe disease (complete acid α-glucosidase defi ciency-related) in two different settings: England and Colombia. Pompe disease is very rare (1:40,000 births incidence). Methods A lit...
- Autores:
-
Castro Jaramillo, Hector Eduardo
- Tipo de recurso:
- Article of journal
- Fecha de publicación:
- 2012
- Institución:
- Universidad Nacional de Colombia
- Repositorio:
- Universidad Nacional de Colombia
- Idioma:
- spa
- OAI Identifier:
- oai:repositorio.unal.edu.co:unal/31342
- Acceso en línea:
- https://repositorio.unal.edu.co/handle/unal/31342
http://bdigital.unal.edu.co/21420/
http://bdigital.unal.edu.co/21420/2/
- Palabra clave:
- evaluación economica en salud
farmacoeconomia
enfermedades huerfanas
enfermedades de alto costo
sistemas de salud
terapia reemplazo enzimatica
Glycogen storage disease type II
Pompe disease
cost and cost analysis
cost- benefi t analysis
quality of life
Economia de salud
Salud Publica
Politicas de salud
Pediatria
- Rights
- openAccess
- License
- Atribución-NoComercial 4.0 Internacional